What Are the RASopathies?

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Learn about the individual RASopathy syndromes

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1:1,000 ?

Individually, each of the RASopathies is rare ~ Together they come close to 1:1,000

 
 

Find a Clinician

Clinicians around the world

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Latest News

BabyMERIT: U.S. Phase 3 Clinical Trial for Infants with RASopathy-Associated Hypertrophic Cardiomyopathy

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The Spark We've Been Waiting For We are ecstatic to share the announcement of BabyMERIT: the first U.S. phase 3 clinical trial to study the MEK inhibitor (Trametinib) in babies…
Share you Noonan syndrome experience with this anonymous research survey

Participants Wanted

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New International Research Survey from Boston Children's Hospital Recruiting participants for an anonymous online survey to explore the symptoms and impact of musculoskeletal pain in Noonan syndrome for adolescents and…

Suspension of BioMarin Clinical Trial of VOXZOGO® (vosoritide) in Noonan Syndrome

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BioMarin has made the decision to discontinue development of VOXZOGO® (vosoritide) for children with Noonan syndrome. Read the press release here.

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